Rare diseases Archives

News & Features

Merck Snaps Up Parkinson’s Candidates For Up to $610M

Malorye Branca -

November 22, 2023

Molecular Dx

Oxford Nanopore and Genomics England to Sequence 7,500 Samples for Rare Disease Initiative

Malorye Branca -

November 3, 2023

News & Features

Metabolon, Genomics England Partner to Advance Rare Disease Diagnosis

Chris Anderson -

October 26, 2023

Female Scientist In Lab to illustrate ASO's being developed by n-Lorem to treat nano-rare diseases

News & Features

n-Lorem to Collaborate with St. Jude Children’s Research Hospital to Accelerate ASO Development

Helen Albert -

October 4, 2023

Colorful rare disease awareness ribbon with a group of different colored sillouettes symbolizing people with rare diseases.

News & Features

Oxford Rare Disease Accelerator Launched to Develop New Treatments

Helen Albert -

October 3, 2023

Asian looking baby with black hair and pale skin showing an outbreak of eczema on their face.

Molecular Dx

Genomics England Releases List of over 200 Rare Conditions for Newborn Screening Study

Malorye Branca -

October 3, 2023

News & Features

FDA Begins Program to Speed Up Development of Rare Disease Therapeutics

Helen Albert -

October 2, 2023

Molecular Dx

Early Rare Disease Diagnosis Could Save as Much as $500,000 per Patient

Chris Anderson -

September 15, 2023

Illustration of a human head and neck showing a cut-through to the brain on the left hand side on a background picture of fluorescent neurons and with a DNA helix to the right hand side to represent genetic brain and neurological disorders such as the movement disorder ataxia.

News & Features

Verge and AZ Ink Potential $840M Drug Discovery Deal

Malorye Branca -

September 8, 2023

News & Features

Rare Disease Shares Same Molecular Mechanism as Cystic Fibrosis

Chris Anderson -

August 29, 2023

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Map of DDX3X Gene Shows Impacts to the Health of Any…

Smear Test Flags Ovarian Cancer

AbbVie Acquires Neuroscience Shop Cerevel for $8.7B

Treatment, versus Monitoring, Improves Outcomes in Grade 2 Cervical Lesions

Protein Previously Implicated in Tumor Growth and Angiogenesis New Pancreatic Cancer…

Rare diseases

Merck Snaps Up Parkinson’s Candidates For Up to $610M

Oxford Nanopore and Genomics England to Sequence 7,500 Samples for Rare Disease Initiative

Metabolon, Genomics England Partner to Advance Rare Disease Diagnosis

n-Lorem to Collaborate with St. Jude Children’s Research Hospital to Accelerate ASO Development

Oxford Rare Disease Accelerator Launched to Develop New Treatments

Genomics England Releases List of over 200 Rare Conditions for Newborn Screening Study

FDA Begins Program to Speed Up Development of Rare Disease Therapeutics

Early Rare Disease Diagnosis Could Save as Much as $500,000 per Patient

Verge and AZ Ink Potential $840M Drug Discovery Deal

Rare Disease Shares Same Molecular Mechanism as Cystic Fibrosis

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AbbVie Acquires Neuroscience Shop Cerevel for $8.7B

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