Genetic diseases Archives

News & Features

Pfizer Gene Therapy for Hemophilia A Nets Positive Results, but Leaves Questions

Malorye Branca -

July 25, 2024

News & Features

Study Finds Higher Rates of Hereditary Cancer Mutations in Minority Populations Missed by Current Screening Guidelines

Alice McCarthy -

July 24, 2024

Genetic engineering concept. DNA. Gene therapy. Medical technology

News & Features

New Gene Therapy for Muscular Dystrophy May Facilitate Development of Others

Camille Mojica Rey, PhD -

July 18, 2024

Neurons sending pulsating electric impulses and communicating with each other. Concept For Neurological Diseases, Tumors And Brain Surgery

News & Features

uniQure’s Potential Breakthrough Gene Therapy for Huntington’s Delivers Positive Trial Results

Malorye Branca -

July 12, 2024

Chromatin strand and isolated nucleosome. DNA (yellow), histones (blue).

News & Features

Protein Action against Jumping Genes Revealed

Anita Chakraverty -

July 12, 2024

News & Features

Gene Editing Could Stave off Deafness

Anita Chakraverty -

July 11, 2024

Man with Duchenne muscular dystrophy sitting in a motorized wheelchair using power controller with degenerated hands

News & Features

Sarepta Wins Key Label Expansion for DMD Gene Therapy, in Wake of Pfizer Failure

Malorye Branca -

June 21, 2024

News & Features

CRISPR Editing Strategy May Eliminate Toxic Conditioning for Cell Therapy

Jonathan D. Grinstein, PhD -

June 20, 2024

News & Features

CASGEVY Is Durable in over 100 Patients, Editas’ Reni-cel Shows Clinical Promise

Jonathan D. Grinstein, PhD -

June 17, 2024

DNA sequence with colored letters on black background containing mutation

Molecular Dx

New Sequencing Technique Unveils Earliest Signs of Genetic Mutations

Alisa Kirkin -

June 13, 2024

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Mini Lungs Reveal More Cells Susceptible to COVID-19

Antimicrobial Susceptibility Test Turnaround Time Slashed by Novel Method

New Therapeutic Target Found for Acute Myeloid Leukemia

Fecal Microbiota Transplants Could Boost Cancer Immunotherapy Efficacy

New Research Shows Potential for Ketone Therapy in Heart Failure

Genetic diseases

Pfizer Gene Therapy for Hemophilia A Nets Positive Results, but Leaves Questions

Study Finds Higher Rates of Hereditary Cancer Mutations in Minority Populations Missed by Current Screening Guidelines

New Gene Therapy for Muscular Dystrophy May Facilitate Development of Others

uniQure’s Potential Breakthrough Gene Therapy for Huntington’s Delivers Positive Trial Results

Protein Action against Jumping Genes Revealed

Gene Editing Could Stave off Deafness

Sarepta Wins Key Label Expansion for DMD Gene Therapy, in Wake of Pfizer Failure

CRISPR Editing Strategy May Eliminate Toxic Conditioning for Cell Therapy

CASGEVY Is Durable in over 100 Patients, Editas’ Reni-cel Shows Clinical Promise

New Sequencing Technique Unveils Earliest Signs of Genetic Mutations

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New Therapeutic Target Found for Acute Myeloid Leukemia

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Passage Bio's Dementia Gene Therapy Trial Expands Patient Pool