Inborn genetic diseases Archives

Sickle Cell disease - 3D Illustration of sickled blood cells on a dark background

News & Features

Can Gene Therapy Be Affordable? U.S. Tries New Access Model in Sickle Cell Disease

Malorye Branca -

February 7, 2024

News & Features

BridgeBio Nabs About $1.25B to Power Genetic Medicine and Cancer Pipeline

Malorye Branca -

January 22, 2024

An illustration of a CRISPR-Cas9 gene editing protein cutting a DNA helix

News & Features

In Another Win for CRISPR, FDA Approves Casgevy for Beta Thalassemia

Malorye Branca -

January 17, 2024

News & Features

Two Gene Therapies for Sickle Cell Disease Get FDA Nod, Including First Ever CRISPR-Based Therapy

Malorye Branca -

December 11, 2023

News & Features

U.K. Approves Vertex/CRISPR Tx’s Casgevy for Sickle Cell and Beta Thalassemia

Malorye Branca -

November 16, 2023

Illustration of the bottom half of a female body showing the bladder and kidneys highlighted with a circle to the right of the image filled with bacteria indicating a urinary tract infection

Molecular Dx

Mycoplasma Protein in Urogenital Tract Linked to Infertility and Birth Defects

Alisa Kirkin -

July 19, 2023

News & Features

Base Editing Is Superior in Lab Test of Sickle Cell Disease Gene Therapy

Malorye Branca -

July 5, 2023

News & Features

One and Done? How CRISPR Is Changing the Clinical Outlook for Multiple Diseases

Kathy Vuksanaj -

June 5, 2023

Illustration of red blood cells moving through clogged artery to indicate cholesterol build up as a result of homozygous familial hypercholesterolemia and atherosclerosis

Molecular Dx

National Screening for Familial Hypercholesterolemia Cost-Effective

Helen Albert -

May 2, 2023

Blood clot made of red blood cells, platelets and fibrin protein strands. Thrombus

News & Features

Bluebird Tightens Sickle Cell Race with BLA for Gene Therapy

Malorye Branca -

April 25, 2023

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Vitamin D May Improve Cancer Immunity by Altering the Gut Microbiome

Do COVID-19 mRNA Vaccines Boost Mucosal Immunity?

Pandemic Preparedness Needs Genomic Surveillance

Walgreens Dives into Gene and Cell Therapy Delivery

A Newly Discovered Tumor Mechanism Could Improve Immunotherapies

Inborn genetic diseases

Can Gene Therapy Be Affordable? U.S. Tries New Access Model in Sickle Cell Disease

BridgeBio Nabs About $1.25B to Power Genetic Medicine and Cancer Pipeline

In Another Win for CRISPR, FDA Approves Casgevy for Beta Thalassemia

Two Gene Therapies for Sickle Cell Disease Get FDA Nod, Including First Ever CRISPR-Based Therapy

U.K. Approves Vertex/CRISPR Tx’s Casgevy for Sickle Cell and Beta Thalassemia

Mycoplasma Protein in Urogenital Tract Linked to Infertility and Birth Defects

Base Editing Is Superior in Lab Test of Sickle Cell Disease Gene Therapy

One and Done? How CRISPR Is Changing the Clinical Outlook for Multiple Diseases

National Screening for Familial Hypercholesterolemia Cost-Effective

Bluebird Tightens Sickle Cell Race with BLA for Gene Therapy

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Walgreens Dives into Gene and Cell Therapy Delivery

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